发明名称 COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
摘要 The invention relates to double-stranded ribonucleic acid (dsRNA) compositions targeting the ALAS1 gene, and methods of using such dsRNA compositions to alter (e.g., inhibit) expression of ALAS1.
申请公布号 PH12016500574(A1) 申请公布日期 2016.05.23
申请号 PH12016500574 申请日期 2016.03.29
申请人 ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI;ALNYLAM PHARMACEUTICALS, INC. 发明人 BETTENCOURT, BRIAN;FITZGERALD, KEVIN;QUERBES, WILLIAM;DESNICK, ROBERT, J;YASUDA, MAKIKO
分类号 A61K31/7088;A61K31/713;A61P3/00;C12N15/113 主分类号 A61K31/7088
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