发明名称 METHOD OF ENHANCING LYSOSOMAL ALPHA-GALACTOSIDASE A
摘要 A method of enhancing the activity of lysosomal ±-Galactosidase A (±-Gal A) in mammalian cells and for treatment of Fabry disease by administration of 1-deoxy-galactonojirimycin and related compounds.
申请公布号 EP1083899(A4) 申请公布日期 2004.11.03
申请号 EP19990925611 申请日期 1999.05.28
申请人 THE MOUNT SINAI SCHOOL OF MEDICINE OF NEW YORK UNIVERSITY 发明人 FAN, JIAN-QIANG;ISHII, SATOSHI
分类号 A61K31/445;A61K31/4465;A61K31/7008;A61K31/7042;A61K31/7052;A61K31/706;A61P43/00;C07D207/12;C07D211/46;C07H17/02;C12N9/40 主分类号 A61K31/445
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