发明名称 |
PRODUCTION OF OVERSIZED ADENO-ASSOCIATED VECTORS |
摘要 |
Provided herein are methods for producing an adeno-associated virus (AAV) particle containing an oversized recombinant AAV genome (e.g., greater than 4.7 kb). In some aspects, the invention provides AAV particles and AAV vectors comprising oversized rAAV genomes. Producer cell lines to produce AAV particles comprising oversized genomes are also provided. |
申请公布号 |
WO2016164609(A2) |
申请公布日期 |
2016.10.13 |
申请号 |
WO2016US26486 |
申请日期 |
2016.04.07 |
申请人 |
GENZYME CORPORATION |
发明人 |
KYOSTIO-MOORE, Sirkka;SOUZA, David;VINCENT, Karen |
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