TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES
摘要
The present invention provides iRNA agents, e.g., double stranded iRNA agents, that target the transthyretin (TTR) gene and methods of using such iRNA agents for treating or preventing TTR-associated diseases.
申请公布号
WO2017023660(A1)
申请公布日期
2017.02.09
申请号
WO2016US44359
申请日期
2016.07.28
申请人
ALNYLAM PHARMACEUTICALS, INC.
发明人
ZIMMERMANN, Tracy;CHAN, Amy;JADHAV, Vasant;MAIER, Martin;RAJEEV, Kallanthottathil, G.
