发明名称 MODULATION AF HUNTINGTIN EKSPRESSION
摘要 Provided herein are methods, compounds, and compositions for reducing expression of huntingtin mRNA and protein in an animal. Such methods, compounds, and compositions are useful to treat, prevent, delay, or ameliorate Huntington's disease, or a symptom thereof.
申请公布号 DK2475675(T3) 申请公布日期 2017.02.06
申请号 DK20100816206T 申请日期 2010.09.10
申请人 Ionis Pharmaceuticals, Inc. 发明人 HUNG, Gene;BENNETT, C., Frank;FREIER, Susan, M.;KORDASIEWICZ, Holly;STANEK, Lisa;CLEVELAND, Don, W.;Cheng, Seng, H.;SHIHABUDDIN, Lamya
分类号 C12N15/113;A61K31/712;A61K31/7125 主分类号 C12N15/113
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