摘要 |
Provided herein are methods, compounds, and compositions for reducing expression of huntingtin mRNA and protein in an animal. Such methods, compounds, and compositions are useful to treat, prevent, delay, or ameliorate Huntington's disease, or a symptom thereof. |
申请人 |
Ionis Pharmaceuticals, Inc. |
发明人 |
HUNG, Gene;BENNETT, C., Frank;FREIER, Susan, M.;KORDASIEWICZ, Holly;STANEK, Lisa;CLEVELAND, Don, W.;Cheng, Seng, H.;SHIHABUDDIN, Lamya |