发明名称 métodos para prevenção e/ou tratamento de doenças de armazenamento lisossomal
摘要 The present invention provides methods for preventing and/or treating lysosomal storage disorders using 5-(fluoromethyl)piperidine-3,4-diol, 5-(chloromethyl)piperidine-3,4-diol, or a pharmaceutically acceptable salt, solvate, or prodrug thereof, or any combination of two or more thereof. In particular, the present invention provides methods for preventing and/or treating Gaucher's disease.
申请公布号 BRPI1010517(A2) 申请公布日期 2017.01.31
申请号 BR2010PI10517 申请日期 2010.04.09
申请人 AMICUS THERAPEUTICS, INC. 发明人 Gary Lee;Robert Boyd
分类号 A61K31/445;A01N43/40 主分类号 A61K31/445
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