发明名称 |
Compound for treatment of myotonic dystrophy type 1 |
摘要 |
The present invention relates to a compound, or a salt thereof, and a pharmaceutical composition comprising said compound, or a salt thereof, for use in the prevention and/or treatment of myotonic dystrophy type 1 in a patient, in particular by reducing the levels of autophagy and apoptosis that are elevated in myotonic muscular dystrophy type 1. |
申请公布号 |
EP3034074(A1) |
申请公布日期 |
2016.06.22 |
申请号 |
EP20140198823 |
申请日期 |
2014.12.18 |
申请人 |
UNIVERSITAT DE VALÈNCIA, ESTUDI GENERAL |
发明人 |
ARTERO ALLEPUZ, RUBÉN DARÍO;BARGIELA SCHÖNBRUNN, ARIADNA;LLAMUSÍ TROÍSI, BEATRIZ;PÉREZ ALONSO, MANUEL;FERNÁNDEZ COSTA, JUAN MANUEL |
分类号 |
A61K31/198;A61K31/4439;A61K31/4709;A61K31/4745;A61P21/00 |
主分类号 |
A61K31/198 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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