发明名称 Compound for treatment of myotonic dystrophy type 1
摘要 The present invention relates to a compound, or a salt thereof, and a pharmaceutical composition comprising said compound, or a salt thereof, for use in the prevention and/or treatment of myotonic dystrophy type 1 in a patient, in particular by reducing the levels of autophagy and apoptosis that are elevated in myotonic muscular dystrophy type 1.
申请公布号 EP3034074(A1) 申请公布日期 2016.06.22
申请号 EP20140198823 申请日期 2014.12.18
申请人 UNIVERSITAT DE VALÈNCIA, ESTUDI GENERAL 发明人 ARTERO ALLEPUZ, RUBÉN DARÍO;BARGIELA SCHÖNBRUNN, ARIADNA;LLAMUSÍ TROÍSI, BEATRIZ;PÉREZ ALONSO, MANUEL;FERNÁNDEZ COSTA, JUAN MANUEL
分类号 A61K31/198;A61K31/4439;A61K31/4709;A61K31/4745;A61P21/00 主分类号 A61K31/198
代理机构 代理人
主权项
地址