THERAPEUTIC USES OF GENOME EDITING WITH CRISPR/Cas SYSTEMS
摘要
Disclosed herein are methods, compositions, and kits for high efficiency, site-specific genomic editing of cells for treating or preventing genetic blood disorders.
申请公布号
WO2016057835(A2)
申请公布日期
2016.04.14
申请号
WO2015US54762
申请日期
2015.10.08
申请人
PRESIDENT AND FELLOWS OF HARVARD COLLEGE;CHILDREN'S MEDICAL CENTER CORPORATION
发明人
MUSUNURU, KIRAN;COWAN, CHAD, A.;ROSSI, DERRICK, J.
