Substituted pyrazolopyrimidines as glucocerebrosidase activators
摘要
Substituted pyrazolopyrimidines and dihydropyrazolopyrimidines and related compounds, their methods of manufacture, compositions containing these compounds, and methods of use of these compounds in treating lysosomal storage disorders such as Gaucher disease are described herein. The compounds are of general Formula (I) in which variables R
申请公布号
AU2011338377(A8)
申请公布日期
2015.10.29
申请号
AU20110338377
申请日期
2011.12.08
申请人
THE UNITED STATES OF AMERICA, AS REPRESENTED BY THE SECRETARY
发明人
MARUGAN, JUAN JOSE;SOUTHALL, NOEL;GOLDIN, EHUD;ZHENG, WEI;PATNAIK, SAMARJIT;SIDRANSKY, ELLEN;MOTABAR, OMID;WESTBROOK, WENDY