发明名称 DOSING REGIMENS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES USING PHARMACOLOGICAL CHAPERONES
摘要 <p>The present invention provides dosing regimens for administering pharmacological chaperones to a subject in need thereof. The dosing regimens can be used to treat disorders caused by improper protein misfolding, such as lysosomal storage disorders.</p>
申请公布号 EP2150254(A4) 申请公布日期 2010.11.10
申请号 EP20080747020 申请日期 2008.04.28
申请人 AMICUS THERAPEUTICS, INC. 发明人 LOCKHART, DAVID;WUSTMAN, BRANDON
分类号 A61K31/44;A61K31/45;A61P43/00 主分类号 A61K31/44
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