发明名称 |
DOSING REGIMENS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES USING PHARMACOLOGICAL CHAPERONES |
摘要 |
<p>The present invention provides dosing regimens for administering pharmacological chaperones to a subject in need thereof. The dosing regimens can be used to treat disorders caused by improper protein misfolding, such as lysosomal storage disorders.</p> |
申请公布号 |
EP2150254(A4) |
申请公布日期 |
2010.11.10 |
申请号 |
EP20080747020 |
申请日期 |
2008.04.28 |
申请人 |
AMICUS THERAPEUTICS, INC. |
发明人 |
LOCKHART, DAVID;WUSTMAN, BRANDON |
分类号 |
A61K31/44;A61K31/45;A61P43/00 |
主分类号 |
A61K31/44 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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