发明名称 |
CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR TREATING USHER SYNDROME AND RETINITIS PIGMENTOSA |
摘要 |
CRISPR/Cas-related compositions and methods for treatment of Usher Syndrome and/or Retinitis Pigmentosa are disclosed herein. |
申请公布号 |
WO2015134812(A1) |
申请公布日期 |
2015.09.11 |
申请号 |
WO2015US19064 |
申请日期 |
2015.03.05 |
申请人 |
EDITAS MEDICINE, INC. |
发明人 |
MAEDER, MORGAN, L.;BUMCROT, DAVID, A. |
分类号 |
C12N15/113;A61K31/7088;A61K48/00;C12N9/22 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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