发明名称 |
METHODS AND COMPOSITIONS FOR THE SPECIFIC INHIBITION OF TRANSTHYRETIN (TTR) BY DOUBLE-STRANDED RNA |
摘要 |
This invention relates to compounds, compositions, and methods useful for reducing transthyretin (TTR) target RNA and protein levels via use of dsRNAs, e.g., Dicer substrate siRNA (DsiRNA) agents. |
申请公布号 |
WO2015085158(A1) |
申请公布日期 |
2015.06.11 |
申请号 |
WO2014US68764 |
申请日期 |
2014.12.05 |
申请人 |
DICERNA PHARMACEUTICALS, INC. |
发明人 |
BROWN, BOD, D.;DUDEK, HENRYK, T. |
分类号 |
C12N15/113;A61K31/7088;C12Q1/68 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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