| 发明名称 |
RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders |
| 摘要 |
The current invention provides an improved oligonucleotide and its use for treating, ameliorating, preventing, delaying and/or treating a human cis-element repeat instability associated genetic neuromuscular or neurodegenerative disorder. |
| 申请公布号 |
EP2841578(A1) |
申请公布日期 |
2015.03.04 |
| 申请号 |
EP20130720617 |
申请日期 |
2013.04.23 |
| 申请人 |
PROSENSA TECHNOLOGIES B.V. |
发明人 |
DE VISSER, PETER CHRISTIAN;MULDERS, SUSAN ALLEGONDA MARIA |
| 分类号 |
C12N15/113;A61K31/7115;A61K31/712;A61K31/7125;A61P25/00 |
主分类号 |
C12N15/113 |
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