发明名称 |
METHODS AND COMPOSITIONS FOR THE SPECIFIC INHIBITION OF ALPHA-1 ANTITRYPSIN BY DOUBLE-STRANDED RNA |
摘要 |
This invention relates to compounds, compositions, and methods useful for reducing a-1 antitrypsin target RNA and protein levels via use of dsRNAs, e.g., Dicer substrate siRNA (DsiRNA) agents. |
申请公布号 |
CA2916499(A1) |
申请公布日期 |
2015.01.08 |
申请号 |
CA20142916499 |
申请日期 |
2014.07.03 |
申请人 |
DICERNA PHARMACEUTICALS, INC. |
发明人 |
BROWN, BOB D.;DUDEK, HENRYK T. |
分类号 |
C12N15/113;A61K31/7088;A61K31/713;A61P1/16;A61P35/00 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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