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发明名称
EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
摘要
Antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon 44 skipping are described.
申请公布号
WO2014153220(A2)
申请公布日期
2014.09.25
申请号
WO2014US29689
申请日期
2014.03.14
申请人
SAREPTA THERAPEUTICS, INC.
发明人
BESTWICK, RICHARD, K.;FRANK, DIANE, ELIZABETH
分类号
C12N15/11
主分类号
C12N15/11
代理机构
代理人
主权项
地址
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