发明名称 |
PYRAZOLOPYRIDAZINES AND METHODS FOR TREATING RETINAL-DEGENERATIVE DISEASES AND HEARING LOSS ASSOCIATED WITH USHER SYNDROME |
摘要 |
Compounds, compositions and methods for the treatment of retinal degenerative diseases, such as retinitis pigmentosa, Leber's congenital Amaurosis, Syndromic retinal degenerations, age-related macular degeneration and Usher Syndrome, and hearing loss associated with Usher Syndrome are described herein. |
申请公布号 |
EP2701510(A4) |
申请公布日期 |
2014.06.11 |
申请号 |
EP20120777328 |
申请日期 |
2012.04.25 |
申请人 |
USHER III INITIATIVE |
发明人 |
BURLI, ROLAND WERNER;ESMIEU, WILLIAM RAMESHCHANDRA KRISHNA;LOCK, CHRISTOPHER JAMES;MALAGU, KARINE FABIENNE;OWENS, ANDREW PATE;HARTE, WILLIAM EDWARD |
分类号 |
A61K31/40;C07C251/86;C07D487/04;C07D519/00 |
主分类号 |
A61K31/40 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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