发明名称 SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
摘要 The invention relates to iRNA, e.g., double-stranded ribonucleic acid (dsRNA), compositions targeting the Serpinc1 gene, and methods of using such iRNA, e.g., dsRNA, compositions to inhibit expression of Serpinc1 and methods of treating subjects having a bleeding disorder, such as a hemophilia.
申请公布号 US2013317081(A1) 申请公布日期 2013.11.28
申请号 US201313837129 申请日期 2013.03.15
申请人 ALNYLAM PHARMACEUTICALS 发明人 AKINC AKIN;SEHGAL ALFICA;TOUDJARSKA IVANKA;FOSTER DONALD;MILSTEIN STUART;BETTENCOURT BRIAN;MAIER MARTIN A.;CHARISSE KLAUS;KUCHIMANCHI SATYANARAYANA;RAJEEV KALLANTHOTTATHIL G.;MONAHARAN MUTHIAH
分类号 C12N15/113 主分类号 C12N15/113
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