发明名称 |
USE OF INHIBITORS OF PORPHOBILINOGEN DEAMINASE IN THE TREATMENT OF CONGENITAL ERYTHROPOIETIC PORPHYRIA |
摘要 |
<p>The invention relates to the use of a compound of general formula (I), wherein R1 and R2 are independently H or C1-C6 alkyl, or R1 and R2 are bound to one another forming an optionally substituted fused benzene ring, R3 is H, C1-C6 alkyl or -CH2-CH(NH2)-COOH and R4 is H, C1-C6 alkyl, or R4 represents (II) or (III) in the preparation of a medicinal product for treating and/or preventing congenital erythropoietic porphyria (CEP).</p> |
申请公布号 |
EP2624829(A1) |
申请公布日期 |
2013.08.14 |
申请号 |
EP20110746212 |
申请日期 |
2011.08.05 |
申请人 |
CENTRO DE INVESTIGACION COOPERATIVA EN BIOCIENCIAS CIC BIOGUNE |
发明人 |
MILLET AGUILAR-GALINDO, OSCAR;LAIN TORRE, ANA |
分类号 |
A61K31/40;A61K31/404;A61K31/4045;A61K31/405;A61P3/00 |
主分类号 |
A61K31/40 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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