发明名称 |
Dual Targeting siRNA Agents |
摘要 |
The invention relates to dual targeting siRNA agents targeting a PCSK9 gene and a second gene, and methods of using dual targeting siRNA agents to inhibit expression of PCSK.9 and to treat PCSK.9 related disorders, e.g., hyperlipidemia.
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申请公布号 |
US2013184324(A1) |
申请公布日期 |
2013.07.18 |
申请号 |
US201013497226 |
申请日期 |
2010.09.22 |
申请人 |
FITZGERALD KEVIN;FRANK-KAMENETSKY MARIA;CHARISSE KLAUS;ALNYLAM PHARMACEUTICALS, INC. |
发明人 |
FITZGERALD KEVIN;FRANK-KAMENETSKY MARIA;CHARISSE KLAUS |
分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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