发明名称 VECTORS AND SEQUENCES FOR THE TREATMENT OF DISEASES
摘要 The present invention provides new sequences, gene constructions, vectors and pharmaceutical compositions for the treatment of diseases and specially, for the treatment of mucopolysaccharidoses.
申请公布号 US2013158104(A1) 申请公布日期 2013.06.20
申请号 US201113703179 申请日期 2011.06.10
申请人 TUBERT FATIMA BOSCH;LOPEZ EDUARD AYUSO;MATIAS ALBERT RUZO;LABORATORIOS DEL DR ESTEVE S.A;UNIVERSIDAD AUTONOMA DE BARCELONA 发明人 TUBERT FATIMA BOSCH;LOPEZ EDUARD AYUSO;MATIAS ALBERT RUZO
分类号 A61K48/00;C12N15/52;C12N15/864 主分类号 A61K48/00
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