发明名称 |
USE OF DELTA TOCOPHEROL FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS |
摘要 |
This disclosure relates generally to the treatment of lysosomal storage disorders. Specifically, the disclosure relates to a novel use of delta tocopherol in the treatment of diseases and conditions related to lysosomal storage disorders. Included in the present disclosure is a method for the modulation of cholesterol recycling. Further, the disclosure relates to conditions such as Niemann-Pick type C disease, Farber disease, Niemann-Pick type A disease, Wolman disease and Tay Sachs disease. Further included in the present disclosure is a method for treating lysosomal storage disorders comprising the administration of delta tocopherol. Further included in the present disclosure is a method for treating lysosomal storage disorders comprising the administration of delta tocopherol in combination with cyclodextrin to a patient in need thereof.
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申请公布号 |
US2013123214(A1) |
申请公布日期 |
2013.05.16 |
申请号 |
US201113810774 |
申请日期 |
2011.07.19 |
申请人 |
ZHENG WEI;MARUGAN JUAN JOSE;LIU KE;SOUTHALL NOEL TERRENCE;AUSTIN CHRISTOPHER P.;THE UNITED STATES OF AMERICA AS REPRESENTED BY THE SECRETARY DEPARTMENT OF HR |
发明人 |
ZHENG WEI;MARUGAN JUAN JOSE;LIU KE;SOUTHALL NOEL TERRENCE;AUSTIN CHRISTOPHER P. |
分类号 |
A61K31/355;A61K31/724;A61K45/06 |
主分类号 |
A61K31/355 |
代理机构 |
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地址 |
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