发明名称 MOLECULES CHIMIQUES INHIBITRICES DU MECANISME D'EPISSAGE POUR TRAITER DES MALADIES RESULTANT D'ANOMALIES D'EPISSAGE.
摘要 The present invention relates to a compound of one of the formulas I to XXI; a pharmaceutical composition comprising at least one such compound; and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly.
申请公布号 FR2926297(B1) 申请公布日期 2013.03.08
申请号 FR20080050144 申请日期 2008.01.10
申请人 CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE CNRS 发明人 TAZI JAMAL;GRIERSON DAVID;MAHUTEAU BETZER FLORENCE
分类号 C07D401/12;A61K31/165;A61K31/415;A61K31/4192;A61K31/4439;A61K31/444;A61K31/472;A61P3/10;A61P7/12;A61P9/10;A61P17/00;A61P25/00;A61P31/18;A61P35/00;C07C237/30;C07D213/73;C07D213/81;C07D217/24;C07D249/04;C07D295/02 主分类号 C07D401/12
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