发明名称 |
MOLECULES CHIMIQUES INHIBITRICES DU MECANISME D'EPISSAGE POUR TRAITER DES MALADIES RESULTANT D'ANOMALIES D'EPISSAGE. |
摘要 |
The present invention relates to a compound of one of the formulas I to XXI; a pharmaceutical composition comprising at least one such compound; and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly. |
申请公布号 |
FR2926297(B1) |
申请公布日期 |
2013.03.08 |
申请号 |
FR20080050144 |
申请日期 |
2008.01.10 |
申请人 |
CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE CNRS |
发明人 |
TAZI JAMAL;GRIERSON DAVID;MAHUTEAU BETZER FLORENCE |
分类号 |
C07D401/12;A61K31/165;A61K31/415;A61K31/4192;A61K31/4439;A61K31/444;A61K31/472;A61P3/10;A61P7/12;A61P9/10;A61P17/00;A61P25/00;A61P31/18;A61P35/00;C07C237/30;C07D213/73;C07D213/81;C07D217/24;C07D249/04;C07D295/02 |
主分类号 |
C07D401/12 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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