The present invention relates to the selective modulation of pre-mRNA splicing, in particular, for that involving alternative splicing in diseaes-related proteins such as those involved in Duschenne's Muscular Dystropy and Spinal Muscular Atrophy.
申请公布号
WO2012138487(A3)
申请公布日期
2012.12.06
申请号
WO2012US30271
申请日期
2012.03.23
申请人
THE BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM;LIU, JING;HU, JIAXIN;COREY, DAVID, R.