发明名称 OLIGONUCLEOTIDE MODULATION OF SPLICING
摘要 The present invention relates to the selective modulation of pre-mRNA splicing, in particular, for that involving alternative splicing in diseaes-related proteins such as those involved in Duschenne's Muscular Dystropy and Spinal Muscular Atrophy.
申请公布号 WO2012138487(A3) 申请公布日期 2012.12.06
申请号 WO2012US30271 申请日期 2012.03.23
申请人 THE BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM;LIU, JING;HU, JIAXIN;COREY, DAVID, R. 发明人 LIU, JING;HU, JIAXIN;COREY, DAVID, R.
分类号 C07H21/02;C12N5/02 主分类号 C07H21/02
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