发明名称 Method of treating gaucher disease
摘要 Therapeutic compositions and methods for treatment of late-onset Gaucher disease are described herein. The compositions comprise compounds having activity as pharmacological chaperones for mutant forms of the beta-glucocerebrosidase. Methods of treatment involve providing therapeutically effective amounts of such compositions to subjects in need thereof.
申请公布号 US8124597(B2) 申请公布日期 2012.02.28
申请号 US20080229445 申请日期 2008.08.22
申请人 MAHURAN DON J.;TROPAK MICHAEL B.;BUTTNER JUSTIN D.;BLANCHARD JAN E.;BROWN ERIC D.;THE HOSPITAL FOR SICK CHILDREN;MCMASTER UNIVERSITY 发明人 MAHURAN DON J.;TROPAK MICHAEL B.;BUTTNER JUSTIN D.;BLANCHARD JAN E.;BROWN ERIC D.
分类号 A61K31/58;A61K31/397;A61K31/54;A61K31/56 主分类号 A61K31/58
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