发明名称 |
RNA INTERFERENCE SUPPRESSION OF NEURODEGENERATIVE DISEASES AND METHODS OF USE THEREOF |
摘要 |
The present invention is directed to small interfering RNA molecules (siRNA) targeted against nucleic acid sequence that encodes huntingtin or ataxin-1, and methods of using these siRNA molecules.
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申请公布号 |
US2011212520(A1) |
申请公布日期 |
2011.09.01 |
申请号 |
US20100963793 |
申请日期 |
2010.12.09 |
申请人 |
UNIVERSITY OF IOWA RESEARCH FOUNDATION |
发明人 |
DAVIDSON BEVERLY L.;XIA HAIBIN;MAO QINWEN;PAULSON HENRY;BOUDREAU RYAN;HARPER SCOTT |
分类号 |
C12N15/63;C07H21/02;C12N5/10;C12N15/113 |
主分类号 |
C12N15/63 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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