发明名称 |
Microutrophin and uses thereof |
摘要 |
A microutrophin containing a utrophin having internal deletions (relative to a native utrophin) in the hinge regions and a C-terminal deletion is provided. Also provided are vectors and compositions useful for delivering the microutrophin for the treatment of muscular disorders, including Duchenne Muscular Dystrophy.
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申请公布号 |
US7771993(B2) |
申请公布日期 |
2010.08.10 |
申请号 |
US20050586890 |
申请日期 |
2005.01.21 |
申请人 |
THE TRUSTEES OF THE UNIVERSITY OF PENNSYLVANIA |
发明人 |
STEDMAN HANSELL H.;SU LEONARD T.;MITCHELL MARILYN A. |
分类号 |
C12N15/00;A61K38/00;C07H21/04;C07K14/47 |
主分类号 |
C12N15/00 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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