The present invention provides chemically modified siRNA compounds that target RTP801 and pharmaceutical compositions comprising same useful for treating microvascular disorders, eye diseases, hearing impairment, neurodegenerative diseases and disorders, spinal cord injury and respiratory conditions.
申请公布号
WO2009116037(A3)
申请公布日期
2010.03.11
申请号
WO2009IL00302
申请日期
2009.03.17
申请人
QUARK PHARMACEUTICALS, INC.;FEINSTEIN, ELENA;SKALITER, RAMI;KALINSKI, HAGAR;METT, IGOR
发明人
FEINSTEIN, ELENA;SKALITER, RAMI;KALINSKI, HAGAR;METT, IGOR