| 摘要 |
The present invention relates to methods, compounds, and compositions for treating or preventing diseases associated with nonsense mutations in an mRNA by administering the compounds or compositions of the present invention. More particularly, the present invention relates to methods, compounds, and compositions for suppressing premature translation termination associated with a nonsense mutation in an mRNA. |
| 申请人 |
PTC THERAPEUTICS, INC.;ALMSTEAD, NEIL;KARP, GARY, M;WILDE, RICHARD;WELCH, ELLEN;CAMPBELL, JEFFREY, A;REN, HONGYU;CHEN, GUANGMING |
发明人 |
ALMSTEAD, NEIL;KARP, GARY, M;WILDE, RICHARD;WELCH, ELLEN;CAMPBELL, JEFFREY, A;REN, HONGYU;CHEN, GUANGMING |
