发明名称 |
ENA NUCLEIC ACID DRUGS MODIFYING SPLICING IN mRNA PRECURSOR |
摘要 |
<p>Oligonucleotides having a nucleotide sequence complementary to nucleotide numbers such as 2571-2607, 2578-2592, 2571-2592, 2573-2592, 2578-2596, 2578-2601 or 2575-2592 of the dystrophin cDNA (Gene Bank accession No. NM_004006.1) and therapeutic agents for muscular dystrophy comprising such oligonucleotides. <IMAGE></p> |
申请公布号 |
EP1568769(A1) |
申请公布日期 |
2005.08.31 |
申请号 |
EP20030774151 |
申请日期 |
2003.11.21 |
申请人 |
MATSUO, MASAFUMI;NONPROFIT ORGANIZATION TRANSLATIONAL RESEARCH ORGANIZATION OF DUCHENNE MUSCULAR DYSTROPHY;TAKESHIMA, YASUHIRO |
发明人 |
MATSUO, MASAFUMI;TAKESHIMA, YASUHIRO;KOIZUMI, MAKOTO |
分类号 |
A61K38/00;A61K48/00;A61P21/04;C07H21/04;C12N15/113;(IPC1-7):C12N15/11;A61K31/708;A61K31/712 |
主分类号 |
A61K38/00 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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