| 发明名称 |
ADENO-ASSOCIATED VIRUS MEDIATED DELIVERY OF C1EI AS A THERAPY FOR ANGIOEDEMA |
| 摘要 |
This invention is directed to a vector which comprises a promoter operably linked to a nucleic acid sequence encoding the human C1 esterase inhibitor or Factor XII. The invention is also directed to a composition comprising the vector and a method of using the vector to treat or prevent hereditary angioedema. |
| 申请公布号 |
WO2016191746(A1) |
申请公布日期 |
2016.12.01 |
| 申请号 |
WO2016US34852 |
申请日期 |
2016.05.27 |
| 申请人 |
CORNELL UNIVERSITY |
发明人 |
CRYSTAL, Ronald, G.;PAGOVICH, Odelya, E.;CHIUCHIOLO, Maria, J. |
| 分类号 |
A61K39/00;A61K39/395;C12N15/861 |
主分类号 |
A61K39/00 |
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