发明名称 |
CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR TREATING LEBER'S CONGENITAL AMAUROSIS 10 (LCA10) |
摘要 |
CRISPR/CAS-related compositions and methods for treatment of Leber's Congenital Amaurosis 10 (LCA10) are disclosed. |
申请公布号 |
EP3116997(A1) |
申请公布日期 |
2017.01.18 |
申请号 |
EP20150714320 |
申请日期 |
2015.03.10 |
申请人 |
Editas Medicine, Inc. |
发明人 |
MAEDER, Morgan, L.;BUMCROT, David, A.;SHEN, Shen |
分类号 |
C12N15/113;A61K31/7088;A61K48/00;C12N9/22;C12N15/86 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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