| 发明名称 |
EXOSOMES USEFUL TO TREAT LYSOSOMAL STORAGE DISEASE |
| 摘要 |
Exosomes which are genetically modified to incorporate a functional lysosomal protein and/or nucleic acid encoding a functional lysosomal protein are provided, as well as the use of such genetically modified exosomes to treat lysosomal storage disease. |
| 申请公布号 |
WO2016044947(A1) |
申请公布日期 |
2016.03.31 |
| 申请号 |
WO2015CA50959 |
申请日期 |
2015.09.25 |
| 申请人 |
EXERKINE CORPORATION |
发明人 |
TARNOPOLSKY, MARK;SAFDAR, ADEEL |
| 分类号 |
C12N5/10;A61K8/00;A61K9/51;A61K38/17;A61K38/47;A61P3/00;C07K14/705;C07K17/04;C12N9/10;C12N9/14;C12N9/24;C12N9/48;C12N11/04 |
主分类号 |
C12N5/10 |
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