发明名称 |
FOLLISTATIN IN TREATING DUCHENNE MUSCULAR DYSTROPHY |
摘要 |
The present invention provides, among other things, methods and compositions for treating muscular dystrophy, in particular, Duchenne muscular dystrophy (DMD). In some embodiments, a method according to the present invention includes administering to an individual who is suffering from or susceptible to DMD an effective amount of a recombinant follistatin protein such that at least one symptom or feature of DMD is reduced in intensity, severity, or frequency, or has delayed onset. |
申请公布号 |
US2016083440(A1) |
申请公布日期 |
2016.03.24 |
申请号 |
US201414762373 |
申请日期 |
2014.01.24 |
申请人 |
SHIRE HUMAN GENETIC THERAPIES, INC. |
发明人 |
Mineau Rochelle |
分类号 |
C07K14/47;A61K38/17 |
主分类号 |
C07K14/47 |
代理机构 |
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代理人 |
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主权项 |
1. A method of treating Duchenne muscular dystrophy (DMD) comprising
administering to an individual who is suffering from or susceptible to DMD an effective amount of a recombinant follistatin protein such that at least one symptom or feature of DMD is reduced in intensity, severity, or frequency, or has delayed onset. |
地址 |
Lexington MA US |