发明名称 COMPOUNDS FOR TREATING SPINAL MUSCULAR ATROPHY
摘要 Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy.
申请公布号 WO2013119916(A3) 申请公布日期 2013.10.24
申请号 WO2013US25292 申请日期 2013.02.08
申请人 PTC THERAPEUTICS, INC.;F. HOFFMANN-LA ROCHE AG 发明人 QI, HONGYAN;CHOI, SOONGYU;DAKKA, AMAL;KARP, GARY, MITCHELL;NARASIMHAN, JANA;NARYSHKIN, NIKOLAI;TURPOFF, ANTHONY, A.;WEETALL, MARIA, L.;WELCH, ELLEN;WOLL, MATTHEW, G.;YANG, TIANLE;ZHANG, NANJING;ZHANG, XIAOYAN;ZHAO, XIN;GREEN, LUKE;PINARD, EMMANUEL;RATNI, HASANE
分类号 A61K31/53;A01N43/90;A61K31/519;C07D239/70 主分类号 A61K31/53
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