| 发明名称 |
RECOMBINANT HUMAN CLN2 PROTEIN AND METHODS OF ITS PRODUCTION AND USE |
| 摘要 |
The present invention relates to a method for treating a patient having disorder characterized by a deficient amount of functional CLN2 protein in the affected cells, which comprises administering to the patient an amount of CLN2 protein effective to reduce or eliminate the symptoms caused by the deficiency in CLN2 protein.
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| 申请公布号 |
US2013273018(A1) |
申请公布日期 |
2013.10.17 |
| 申请号 |
US201213598556 |
申请日期 |
2012.08.29 |
| 申请人 |
LOBEL PETER;SLEAT DAVID;UNIVERSITY OF MEDICINE AND DENTISTRY OF NEW JERSEY |
发明人 |
LOBEL PETER;SLEAT DAVID |
| 分类号 |
A61K38/43;C12N15/09;A61K38/46;A61K38/48;A61K47/24;A61P25/00 |
主分类号 |
A61K38/43 |
| 代理机构 |
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