| 发明名称 |
TREATMENT OF FRATAXIN (FXN) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO FXN |
| 摘要 |
The present invention relates to antisense oligonucleotides that modulate the expression of and/or function of Frataxin (FXN), in particular, by targeting natural antisense polynucleotides of Frataxin (FXN). The invention also relates to the identification of these antisense oligonucleotides and their use in treating diseases and disorders associated with the expression of FXN. |
| 申请公布号 |
WO2012170771(A1) |
申请公布日期 |
2012.12.13 |
| 申请号 |
WO2012US41484 |
申请日期 |
2012.06.08 |
| 申请人 |
CURNA, INC.;COLLARD, JOSEPH;KHORKOVA SHERMAN, OLGA |
发明人 |
COLLARD, JOSEPH;KHORKOVA SHERMAN, OLGA |
| 分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
| 代理机构 |
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