发明名称 SMALL MOLECULE CONJUGATES FOR INTRACELLULAR DELIVERY OF BIOLOGICALLY ACTIVE COMPOUNDS
摘要 The invention provides novel compounds and conjugates of these compounds useful for the delivery of biologically active substances. Further novel design criteria for chemically stabilized siRNA particular useful when covalently attached to a delivery polymer to achieve in vivo mRNA knock down are disclosed therein.
申请公布号 WO2012089602(A1) 申请公布日期 2012.07.05
申请号 WO2011EP73718 申请日期 2011.12.22
申请人 F. HOFFMANN-LA ROCHE AG;HADWIGER, PHILIPP;HOFFMANN, TORSTEN;JAHN-HOFMANN, KERSTIN;KITAS, ERIC A.;LEWIS, DAVID L.;MOHR, PETER;MUELLER, HANS MARTIN;OTT, GUENTHER;ROEHL, INGO;ROZEMA, DAVID B. 发明人 HADWIGER, PHILIPP;HOFFMANN, TORSTEN;JAHN-HOFMANN, KERSTIN;KITAS, ERIC A.;LEWIS, DAVID L.;MOHR, PETER;MUELLER, HANS MARTIN;OTT, GUENTHER;ROEHL, INGO;ROZEMA, DAVID B.
分类号 C12N15/87;A61K31/713;A61K47/18;A61K48/00;C12N15/11 主分类号 C12N15/87
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