mRNA FOR USE IN TREATMENT OF HUMAN GENETIC DISEASES
摘要
Compositions for modulating the expression of a protein in a target cell comprising at least one RNA molecule which comprises at least one modification conferring stability to the RNA, as well as related methods, are disclosed.
申请公布号
WO2012075040(A2)
申请公布日期
2012.06.07
申请号
WO2011US62459
申请日期
2011.11.29
申请人
SHIRE HUMAN GENETIC THERAPIES, INC.;GUILD, BRAYDON, CHARLES;HEARTLEIN, MICHAEL
