<p>Disclosed is a drug which efficiently allows skipping of the 53rd exon in the human dystrophin gene. Disclosed is an oligomer which makes possible skipping of the 53rd exon of the human dystrophin gene.</p>
申请公布号
WO2012029986(A1)
申请公布日期
2012.03.08
申请号
WO2011JP70318
申请日期
2011.08.31
申请人
NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY;WATANABE, NAOKI;SATOU, YOUHEI;TAKEDA, SHIN'ICHI;NAGATA, TETSUYA