发明名称 CHEMICAL MOLECULES THAT INHIBIT THE SLICING MECHANISM FOR TREATING DISEASES RESULTING FROM SPLICING ANOMALIES
摘要 The present invention relates to a compound of one of the formulas I to XXI; a pharmaceutical composition comprising at least one such compound; and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly.
申请公布号 US2011053975(A1) 申请公布日期 2011.03.03
申请号 US20090811931 申请日期 2009.01.12
申请人 CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE (CNRS;INSTITUT CURIE;UNIVERSITE MONTPELLIER 2 SCIENCES ET TECHNIQUES 发明人 TAZI JAMAL;GRIERSON DAVID;MAHUTEAU-BETZER FLORENCE;ROUX PIERRE
分类号 A61K31/4709;A61K31/4164;A61K31/4192;A61K31/4439;A61K31/444;A61P31/12;C07D211/72;C07D213/72;C07D217/22;C07D249/04;C07D401/12;C07D401/14 主分类号 A61K31/4709
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