| 发明名称 |
Methods And Compositions For Use In Gene Therapy for Treatment of Hemophilia |
| 摘要 |
The invention includes a composition comprising a recombinant adeno-associated viral vector comprising at least two adeno-associated virus inverted terminal repeats, a promoter/regulatory sequence, isolated DNA encoding Factor IX and accompanying 5' and 3' untranslated regions and a transcription termination
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| 申请公布号 |
US2008213222(A1) |
申请公布日期 |
2008.09.04 |
| 申请号 |
US20070932017 |
申请日期 |
2007.10.31 |
| 申请人 |
THE CHILDREN'S HOSPITAL OF PHILADELPHIA |
发明人 |
HIGH KATHERINE A.;HERZOG ROLAND W. |
| 分类号 |
A61K45/00;A61K48/00;A61K38/43;A61K38/48;C12N7/01;C12N9/64;C12N15/00;C12N15/864 |
主分类号 |
A61K45/00 |
| 代理机构 |
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代理人 |
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| 主权项 |
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| 地址 |
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