发明名称 |
TREATMENT OF ALPHA-GALACTOSIDASE A DEFICIENCY |
摘要 |
The invention provides methods of treating alpha galactosidase A deficiency. Dosage forms, methods of administration, and methods of analyzing human alpha galactosidase A are also included. |
申请公布号 |
EP1503788(A4) |
申请公布日期 |
2008.09.03 |
申请号 |
EP20030726489 |
申请日期 |
2003.04.25 |
申请人 |
SHIRE HUMAN GENETIC THERAPIES, INC. |
发明人 |
TRECO, DOUGLAS, A.;LOVEDAY, KENNETH;BOROWSKI, MARIANNE |
分类号 |
C12N15/09;A61K35/16;A61K38/12;A61K38/46;A61K38/47;A61P9/00;A61P13/12;A61P25/04;A61P43/00;C12Q1/34;C12Q1/54 |
主分类号 |
C12N15/09 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|