发明名称 ENA NUCLEIC ACID PHARMACEUTICALS CAPABLE OF MODIFYING SPLICING OF MRNA PRECURSORS
摘要 Oligonucleotides having a nucleotide sequence complementary to nucleotide numbers such as 2571-2607, 2578-2592, 2571-2592, 2573-2592, 2578-2596, 2578-2601 or 2575-2592 of the dystrophin cDNA (Gene Bank accession No. NM_004006.1) and therapeutic agents for muscular dystrophy comprising such oligonucleotides. <IMAGE>
申请公布号 CA2942791(A1) 申请公布日期 2004.06.10
申请号 CA20032942791 申请日期 2003.11.21
申请人 MATSUO, MASAFUMI;TAKESHIMA, YASUHIRO;DAIICHI SANKYO COMPANY, LIMITED;ORPHAN DISEASE TREATMENT INSTITUTE CO., LTD. 发明人 MATSUO, MASAFUMI;TAKESHIMA, YASUHIRO;KOIZUMI, MAKOTO
分类号 C12N15/113;A61K38/00;A61K48/00;A61P21/04;C07H21/00;C07H21/04 主分类号 C12N15/113
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