发明名称 |
ADENOVIRAL VECTORS FOR TREATMENT OF HEMOPHILIA |
摘要 |
An adenoviral vector including at least one DNA sequence encoding a clotting factor, such as, for example, Factor VIII, or Factor IX. Such vectors may be administered to a host in an amount effective to treat hemophilia in the host. The vectors infect hepatocytes very efficiently, whereby the hepatocytes express the DNA sequence encoding the clotting factor.
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申请公布号 |
US2002064812(A1) |
申请公布日期 |
2002.05.30 |
申请号 |
US19980150811 |
申请日期 |
1998.09.10 |
申请人 |
CONNELLY SHEILA;KALEKO MICHAEL;SMITH THEODORE |
发明人 |
CONNELLY SHEILA;KALEKO MICHAEL;SMITH THEODORE |
分类号 |
C12N15/09;A61K31/70;A61K35/76;A61K48/00;A61P7/04;C07K14/755;C12N5/10;C12N9/64;C12N15/861;C12P21/02;C12R1/91;C12R1/92;(IPC1-7):C12P21/06;C07H21/04;C12N15/00;C12N15/63;C12N15/86;C12P21/06;A01N65/00;A01N63/00 |
主分类号 |
C12N15/09 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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