| 发明名称 |
MODULERING AF BCL11A TIL BEHANDLING AF HÆMOGLOBINOPATIER |
| 摘要 |
The invention relates to methods and uses of modulating fetal hemoglobin expression (HbF) in a hematopoietic progenitor cells via inhibitors of BCL11A expression or activity, such as RNAi and antibodies. |
| 申请公布号 |
DK2334794(T3) |
申请公布日期 |
2017.02.20 |
| 申请号 |
DK20090813730T |
申请日期 |
2009.09.14 |
| 申请人 |
Children's Medical Center Corporation;President and Fellows of Harvard College |
发明人 |
ORKIN, Stuart, H.;SANKARAN, Vijay, G. |
| 分类号 |
C12N15/63;A61K31/7088;C12N15/113 |
主分类号 |
C12N15/63 |
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