发明名称 METHODS FOR TREATING UREA CYCLE DISORDERS TO PREVENT HYPERAMMONEMIC CRISES BY CONTROLLING BLOOD AMMONIA LEVELS
摘要 The present disclosure provides methods for preventing hyperammonemia crises (HACs) in subjects with a urea cycle disorder (UCD) and for optimizing and adjusting nitrogen scavenging drug dosage for subjects with UCDs to prevent HACs.
申请公布号 WO2015187641(A1) 申请公布日期 2015.12.10
申请号 WO2015US33700 申请日期 2015.06.02
申请人 HORIZON THERAPEUTICS, INC. 发明人 SCHARSCHMIDT, BRUCE;MOKHTARANI, MASOUD
分类号 A61K49/00 主分类号 A61K49/00
代理机构 代理人
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