发明名称 |
ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF |
摘要 |
An antisense molecule capable of binding to a selected target site to induce exon skipping in the dystrophin gene, as set forth in SEQ ID NO: 1 to 202.
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申请公布号 |
US2013274313(A1) |
申请公布日期 |
2013.10.17 |
申请号 |
US201313826880 |
申请日期 |
2013.03.14 |
申请人 |
THE UNIVERSITY OF WESTERN AUSTRALIA |
发明人 |
WILTON STEPHEN DONALD;FLETCHER SUE;MCCLOREY GRAHAM |
分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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