发明名称 SERPINA1 SIRNAS: COMPOSITIONS OF MATTER AND METHODS OF TREATMENT
摘要 The technology described herein relates to double-stranded ribonucleic acid (dsRNA) compositions targeting the Serpina1 gene, and methods of using such dsRNA compositions to inhibit expression of Serpina1.
申请公布号 WO2012178033(A2) 申请公布日期 2012.12.27
申请号 WO2012US43782 申请日期 2012.06.22
申请人 ALNYLAM PHARMACEUTICALS, INC.;SEHGAL, ALFICA;BUMCROT, DAVID;BETTENCOURT, BRIAN 发明人 SEHGAL, ALFICA;BUMCROT, DAVID;BETTENCOURT, BRIAN
分类号 A61K48/00;A61K38/17 主分类号 A61K48/00
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