MEDICAL PREPARATIONS FOR THE TREATMENT OF ALPHA-GALACTOSIDASE A DEFICIENCY
摘要
The invention provides highly purified ±-Gal A, and various methods for purifying it; ±-Gal A preparations with altered charge and methods for making those preparations; ±-Gal A preparations that have an extended circulating half-life in a mammalian host, and methods for making same; and methods and dosages for administering an ±-Gal A preparation to a subject.
申请公布号
EP2314699(A1)
申请公布日期
2011.04.27
申请号
EP20100180768
申请日期
2000.03.09
申请人
SHIRE HUMAN GENETIC THERAPIES, INC.
发明人
SELDEN, RICHARD F;BOROWSKI, MARIANNE;KINOSHITA, CAROL M;TRECO, DOUGLAS A;WILLIAMS, MELANIE D;SCHUETZ, THOMAS J;DANIEL, PETER FRANCIS