发明名称 |
SELF DELIVERING BIO-LABILE PHOSPHATE PROTECTED PRO-OLIGOS FOR OLIGONUCLEOTIDE BASED THERAPEUTICS AND MEDIATING RNA INTERFERENCE |
摘要 |
Disclosed herein are compositions and methods for generating ribo-nucleic neutral (RNN) or deoxyribo-nucleic-neutral (DNN) polynucleotides with reduced anionic charge, for improved intracellular delivery. Also disclosed herein are methods of using RNN and DNN compositions. |
申请公布号 |
WO2010039543(A3) |
申请公布日期 |
2010.10.07 |
申请号 |
WO2009US58064 |
申请日期 |
2009.09.23 |
申请人 |
TRAVERSA THERAPEUTICS, INC.;PETERSEN, SCOTT, G. |
发明人 |
PETERSEN, SCOTT, G. |
分类号 |
C07F9/06;A61K48/00;C07F9/576;C07F9/58;C07F9/655;C07F9/6561;C07H21/02;C12N15/113 |
主分类号 |
C07F9/06 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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